Timeline: The Orphan Drug Act

KHN Original

Follow the twists and turns of the orphan drug industry over the past three decades.

Interactive: How Orphan Drugs Win The ‘Monopoly’ Game

KHN Original

Check out all the drugs the FDA has approved to treat rare diseases. You can search by brand name, or by disease, and see familiar names that were first sold on the mass market or all the drugs that won FDA approval to treat more than one rare disease.

Long-Stalled FDA Reform Sits On Senate’s Lame-Duck Calendar

KHN Original

The legislation would give federal officials more flexibility in evaluating the effectiveness and safety of drugs and devices and add billions of dollars to NIH funding. But critics say it could endanger patients’ safety and doesn’t do enough to stop spiraling drug prices.